PubMed ID: 42642361
Author(s): Pattnaik BR, Sahel JA. Reprogramming translation for rare disease therapy: challenges posed by large genes. Signal Transduct Target Ther. 2026 Aug 26;11(1):349. doi: 10.1038/s41392-026-02942-8. No abstract available. PMID 42642361
Journal: Signal Transduction And Targeted Therapy, Volume 11, Issue 1, Aug 2026