Choroideremia (CHM) Health Outcomes
Kimberly Stepien
Pro-EYS
Rate of Progression in EYS Related Retinal Degeneration (Pro-EYS).
AGTC A3
A Multiple-Site, Phase 1/2, Safety and Efficacy Trial of AGTC 402, a Recombinant Adeno-associated Virus Vector Expressing CNGA3, in Patients with Congenital Achromatopsia Caused by Mutations in the CNGA3 Gene
AGTC B3
A Multiple-Site, Phase 1/2, Safety and Efficacy Trial of a Recombinant Adeno-associated Virus Vector Expressing CNGB3 (rAAV2tYF-PR1.7-hCNGB3) in Patients with Congenital Achromatopsia Caused by Mutations in the CNGB3 Gene
NIGHT
Natural History of the Progression of Choroideremia Study (NIGHT)
STAR
A Randomized, Open Label, Outcomes-Assessor Masked, Prospective, Parallel Controlled Group, Phase 3 Clinical Trial of Retinal Gene Therapy For Choroideremia Using An Adeno-Associated Viral Vector (AAV2) Encoding Rab Escort Protein 1 (REP1) (STAR)
SOLSTICE
A Long-term Follow-up Study to Evaluate the Safety and Efficacy of Retinal Gene Therapy in Subjects with Choroideremia Treated Previously with Adeno-Associated Viral Vector Encoding Rab Escort Protein-1 (AAV2-REP1) in an Antecedent Study (SOLSTICE)
Alcohol Pads and Nonsterile Gloves in Preparation of Aflibercept.
PubMed ID: 32768034 Author(s): Regan KA, Gottlieb JL, Altaweel MM, Mititelu M, Blodi BA, Nork TM, Stepien KE, Chang JS. Alcohol pads and nonsterile gloves in preparation of aflibercept. Ophthalmol Retina. 2020 Aug;4(8):853-854. doi: 10.1016/j.oret.2020.04.006. …
Retinal Toxicity in a Patient on Pentosan Polysulfate Sodium.
PubMed ID: 32305545 Author(s): Wingelaar MJ, Raevis JJ, Conlin KA, Stepien KE. Retinal toxicity in a patient on pentosan polysulfate sodium. Urology. 2020 Jul;141:e41-e42. doi: 10.1016/j.urology.2020.04.006. Epub 2020 Apr 17. PMID 32305545 Journal: Urology, Volume …